Sarepta Therapeutics
Sarepta Therapeutics is a biotechnology company specializing in precision genetic medicine for rare diseases, with over 40 investigational therapies and FDA-approved treatments for Duchenne muscular dystrophy.
Services
Sarepta Therapeutics provides specialized services focused on developing precision genetic medicine for rare diseases. It offers FDA-approved treatments for Duchenne muscular dystrophy and operates a gene therapy engine to create new therapies for debilitating illnesses. In addition to its medical services, the company offers a patient support program in the United States called SareptAssist.
Products
Sarepta Therapeutics has a range of products primarily aimed at treating rare diseases. The company's portfolio includes FDA-approved therapies specifically designed for Duchenne muscular dystrophy. These treatments are the result of its commitment to innovation in gene therapy, RNA technologies, and gene editing modalities.
Research and Development
With over 40 investigational therapies in various stages of development, Sarepta Therapeutics is at the forefront of genetic medicine. The company's research employs advanced gene therapy, RNA technologies, and gene editing modalities. It maintains a strong focus on developing new treatments through its gene therapy engine, constantly working on therapies for devastating diseases.
Global Presence
Sarepta Therapeutics has established a significant global presence with offices and operations in multiple countries, including the United States, Ireland, Switzerland, and the United Kingdom. This international footprint allows the company to expand its reach and impact, facilitating collaborations and advancing its mission on a global scale.
Corporate Responsibility
Sarepta Therapeutics is committed to corporate responsibility, which encompasses initiatives in environmental stewardship, people, culture, and governance. These efforts reflect the company's dedication to maintaining high ethical standards and contributing positively to the communities and environments where it operates.